Our Scientific Presentations
Who We Are
A Shared Vision
A new class
of gene therapy.
We’re pushing the limits of genetic medicine.
And our goal is no limits.
liver disease programs.
See our retina
Broad Therapeutic Reach.
Let’s hear it for fuller lives and fewer doctor appointments.
Delve into the possibilities unlocked by our closed-ended DNA.
We see a new reality in genetic medicine ahead.
Focused on leaving nobody behind.
Our non-viral delivery can target specific cells while treating more people.
If you can drastically improve lives, you won’t want to stop at a few thousand.
See the unlimited potential of our capsid-free manufacturing.
Take a seat at the table.
We are always looking for those who are ready to share their vision, talent, and tenacity—who believe in our mission and themselves.
Imagine a world without genetic disease.
What do you see? More health? Fewer doctor appointments? More bike riding? More peanut butter and jelly sandwiches? More life?
See our shared vision.