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A Shared Vision
the limits of
And our goal is no limits.
liver disease programs.
See our retina
Broad Therapeutic Reach.
Let’s hear it for fuller lives and fewer doctor appointments.
Delve into the possibilities unlocked by our immune-quiet DNA.
We see a new reality in genetic medicine ahead.
Focused on leaving nobody behind.
Our non-viral delivery can target specific cells while treating more people.
If you can drastically improve lives, you won’t want to stop at a few thousand.
See the unlimited potential of our rapid enzymatic synthesis.
Take a seat at the table.
We are always looking for those who are ready to share their vision, talent, and tenacity—who believe in our mission and themselves.
Imagine a world without genetic disease.
What do you see? More health? Fewer doctor appointments? More bike riding? More peanut butter and jelly sandwiches? More life?
See our shared vision.