re: Generation

Moving forward: How our new space powers our mission to bring next generation gene therapies to patients
Although we do affectionately refer to it as “301,” our new headquarters is more than an address. It’s an integral part of who we are, what we value, and what we aim to achieve.
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Bringing the light of gene therapy to more patients
Thomas Edison’s first lightbulb in 1879 sparked a revolution. Using electricity that was passed through a platinum filament, his glass bulb required less power than the existing lamps of the day. But it also lasted only a few hours before burning out.
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Genetic diseases steal too many kids' futures. It doesn’t have to be this way.
by GEOFF MCDONOUGH, MD, President & Chief Executive Officer and DOUG KERR, MD, PhD, MBA, Chief Development Officer
This piece was originally published on WBUR’s Cognoscenti. I want to live in a world where children have never heard of hemophilia or cystic fibrosis, because we have all but eradicated those diseases.
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Right from the beginning: returning to the origins of the orphan drug movement
This article was originally published as part of the From The Trenches feature of LifeSciVC. Our industry stands at the beginning of the most significant opportunity to impact genetic and metabolic disease we have ever encountered –
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Take a seat at the table.

We are always looking for those who are ready to share their vision, talent, and tenacity—who believe in our mission and themselves.

Imagine a world without genetic disease.

What do you see? More health? Fewer doctor appointments? More bike riding? More peanut butter and jelly sandwiches? More life?
See our shared vision.