Moving forward: How our new space powers our mission to bring next generation gene therapies to patients
by SARA DEN BESTEN, HEAD OF HUMAN RESOURCES
and PAT MAROLDA, VP OF FACILITIES OPERATIONS AND EH&S
Although we do affectionately refer to it as “301,” our new headquarters is more than an address. It’s an integral part of who we are, what we value, and what we aim to achieve.
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Bringing the light of gene therapy to more patients
by GEOFF MCDONOUGH, MD, PRESIDENT & CHIEF EXECUTIVE OFFICER
and DOUG KERR, MD, PhD, MBA, CHIEF DEVELOPMENT OFFICER
Thomas Edison’s first lightbulb in 1879 sparked a revolution. Using electricity that was passed through a platinum filament, his glass bulb required less power than the existing lamps of the day.
But it also lasted only a few hours before burning out.
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Genetic diseases steal too many kids' futures. It doesn’t have to be this way.
by GEOFF MCDONOUGH, MD, President & Chief Executive Officer and DOUG KERR, MD, PhD, MBA, Chief Development Officer
This piece was originally published on WBUR’s Cognoscenti.
I want to live in a world where children have never heard of hemophilia or cystic fibrosis, because we have all but eradicated those diseases.
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Right from the beginning: returning to the origins of the orphan drug movement
by GEOFF MCDONOUGH, MD, PRESIDENT & CHIEF EXECUTIVE OFFICER
This article was originally published as part of the From The Trenches feature of LifeSciVC.
Our industry stands at the beginning of the most significant opportunity to impact genetic and metabolic disease we have ever encountered –
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